antisense oligonucleotides News

Latest Articles

• St. Jude Scientists Use Synthetic Nucleic Acids to Reverse Ultrarare Neurodevelopmental Disorder in Preclinical Models

  Published: Apr 23, 2026

  Section: Health

  Researchers at St. Jude Children’s Research Hospital have successfully utilized antisense oligonucleotides to reverse symptoms of HNRNPH2-related neurodevelopmental disorder in ani...

• Critical Path Institute Launches One to Millions Initiative to Standardize and Scale Individualized Genetic Therapies for Rare Diseases

  Published: Mar 27, 2026

  Section: Science & Tech

  The Critical Path Institute has introduced "One to Millions," a global public-private partnership designed to modernize regulatory and reimbursement frameworks for highly individua...

• Targeting Specific Protein Fragments May Be Key to Treating Huntington’s Disease According to New Mouse Study

  Published: Mar 18, 2026

  Section: Science & Tech

  Research from the University of Washington School of Medicine suggests that experimental treatments for Huntington’s disease must target a specific toxic fragment called huntingtin...